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Ultragenyx Aligns With FDA On Phase 3 Study Endpoints For GTX-102; Phase 3 Study To Initiate By Year-End; Successful End-Of-Phase 2 Meeting Supports Plans For Global Double-Blind Sham-Controlled Pivotal Study; Additional Study Planned For Patients With Other Mutations

Author: Benzinga Newsdesk | July 17, 2024 04:06pm

Posted In: RARE

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