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News

OPINIONS

 ionis-pharmaceuticals-to-expedite-development-of-rare-neurological-disease-candidate-with-fda-breakthrough-status

FDA designates Ionis Breakthrough Therapy for Angelman syndrome after Phase 1/2 results showed functional improvements.

 hc-wainwright--co-reiterates-buy-on-ultragenyx-pharmaceutical-maintains-80-price-target

HC Wainwright & Co. analyst Raghuram Selvaraju reiterates Ultragenyx Pharmaceutical (NASDAQ:RARE) with a Buy and maintai...

 ultragenyx-reports-96-week-phase-3-results-for-dtx401-in-gsdia-showing-greater-reductions-in-cornstarch-use-and-sustained-glycemic-control

At Week 96 participants experienced even greater reductions in daily cornstarch intake while maintaining low levels of hypoglyc...

 cantor-fitzgerald-reiterates-overweight-on-ultragenyx-pharmaceutical-maintains-105-price-target

Cantor Fitzgerald analyst Kristen Kluska reiterates Ultragenyx Pharmaceutical (NASDAQ:RARE) with a Overweight and maintains ...

 fda-outlines-process-to-speed-up-rare-disease-therapy-approvals

FDA launches Rare Disease Evidence Principles to guide therapy reviews, offering new pathways for approval while raising questi...

 canaccord-genuity-maintains-buy-on-ultragenyx-pharmaceutical-lowers-price-target-to-128

Canaccord Genuity analyst Whitney Ijem maintains Ultragenyx Pharmaceutical (NASDAQ:RARE) with a Buy and lowers the price tar...

 cantor-fitzgerald-maintains-overweight-on-ultragenyx-pharmaceutical-lowers-price-target-to-105

Cantor Fitzgerald analyst Kristen Kluska maintains Ultragenyx Pharmaceutical (NASDAQ:RARE) with a Overweight and lowers the ...

 ultragenyx-pharmaceutical-affirms-fy2025-sales-guidance-of-64000m-67000m-vs-65327m-est

Ultragenyx Pharmaceutical (NASDAQ:RARE) affirms FY2025 sales outlook from $640.00 million-$670.00 million to $640.00 million-$6...

 ultragenyx-pharmaceutical-q2-eps-117-beats-132-estimate-sales-16650m-beat-16250m-estimate

Ultragenyx Pharmaceutical (NASDAQ:RARE) reported quarterly losses of $(1.17) per share which beat the analyst consensus estimat...

 ultragenyx-represents-intriguing-buying-opportunity-despite-recent-setbacks

HC Wainwright initiates Ultragenyx at Buy with $80 target, citing strong rare disease pipeline and late-stage data expected by ...

 hc-wainwright--co-assumes-ultragenyx-pharmaceutical-at-buy-announces-price-target-of-80

HC Wainwright & Co. analyst Raghuram Selvaraju assumes Ultragenyx Pharmaceutical (NASDAQ:RARE) with a Buy rating and ann...

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